Substance / Medication

Naxitamab

Overview

Active Ingredient
naxitamab
RxNorm CUI
2474039

Indications

DANYELZA is indicated, in combination with granulocyte-macrophage colony-stimulating factor (GM-CSF), for the treatment of pediatric patients 1 year of age and older and adult patients with relapsed or refractory high-risk neuroblastoma in the bone or bone marrow who have demonstrated a partial response, minor response, or stable disease to prior therapy. Clinical Studies (14) [see] This indication is approved under accelerated approval based on overall response rate and duration of response. Co

Labeler: Y-mAbs Therapeutics, Inc.Updated: 2025-09-03T00:00:00.000ZFull label on DailyMed

Contraindications

When this intervention should not be used

Warnings and Precautions (5.1) [see]. DANYELZA is contraindicated in patients with a history of severe hypersensitivity reaction to naxitamab-gqgk. Reactions have included anaphylaxis

Indications & Related Conditions

Conditions associated via SNOMED clinical relationships

Administration & Protocol

Dosing, route, and treatment protocol

Detailed dosage and administration information is available in the full FDA drug label.

View full prescribing information on DailyMed

Monitoring & Follow-Up

Biomarkers relevant to this intervention via related conditions

No monitoring biomarkers have been mapped yet. Biomarker-intervention linkages are derived through related conditions and will expand as the knowledge graph grows.

Clinical Trials

11 trials linked to this intervention

11
Total Trials
10
Recruiting
1
With Results

Research Evidence

Published studies and systematic reviews

Sort:
Partial Response to Naxitamab for Brain Metastasis in Neuroblastoma.
Onyeukwu Chinyere, Williams Autumn, Seyboth Brian et al. · J Pediatr Hematol Oncol · 2024
PMID: 38189408Case Report
High-risk neuroblastoma in Mexico: from multimodal treatment to immunotherapy. Regarding the first case treated with naxitamab.
Olaya Vargas Alberto, Salazar-Rosales Haydee, Caballero-Palacios Marcela et al. · Front Oncol · 2025
PMID: 40606987ReviewFull text (PMC)
Naxitamab-combination Therapy for the Treatment of Patients With Refractory and/or Relapsed High-risk Neuroblastoma.
Trovillion Erin Murphy, Michael Meghan, Brown Lauren et al. · J Pediatr Hematol Oncol · 2025
PMID: 40793753Other
Real-life Use of IV Naxitamab for Children With Relapsed/Refractory Neuroblastoma.
Fried Iris, Weintraub Michael, Waldman Dalia et al. · J Pediatr Hematol Oncol · 2025
PMID: 40704649Other
The anti-GD2 monoclonal antibody naxitamab plus GM-CSF for relapsed or refractory high-risk neuroblastoma: a phase 2 clinical trial.
Mora Jaume, Chan Godfrey C F, Morgenstern Daniel A et al. · Nat Commun · 2025
PMID: 39952926TrialFull text (PMC)
A Phase II Trial of Naxitamab plus Stepped-up Dosing of GM-CSF for Patients with High-Risk Neuroblastoma in First Complete Remission.
Kushner Brian H, Modak Shakeel, Mauguen Audrey et al. · Clin Cancer Res · 2025
PMID: 40067131Trial

Research data from MEDLINE/PubMed

Benefits & Expected Outcomes

Benefits, expected outcomes, efficacy data, and NNT (Number Needed to Treat) are pending physician authorship and evidence review.

Risks & Side Effects

Adverse reaction and safety data for this drug is sourced from the FDA-approved label.

View adverse reactions & drug interactions on DailyMed

Related Symptoms

Symptoms associated with conditions this intervention addresses

No related symptoms have been mapped yet. Symptom linkages are derived through associated conditions.

Alternatives & Comparisons

Alternative treatments, comparison data, and clinical decision support are pending physician authorship.

Medical Disclaimer

This information is for educational purposes only and does not constitute medical advice, diagnosis, or treatment. Always consult with a qualified healthcare provider regarding any medical condition or treatment plan.

Do not start, stop, or change any treatment without consulting your healthcare provider.

Quick Facts

Type
Substance / Medication
Fully Specified Name
Naxitamab (substance)
SNOMED CT
1137637004
UMLS CUI
C4733494
RxNorm CUI
2474039
Labeler
Y-mAbs Therapeutics, Inc.

Clinical Data

This intervention maps to 1 entities in the Ltrl knowledge graph.

1
Conditions
0
Biomarkers
0
Specialists
0
Symptoms
11
Clinical Trials

Data is sourced from SNOMED CT, UMLS, and the Ltrl clinical knowledge graph. Content sections marked as pending require physician authorship. Consult a healthcare provider before starting any treatment.